Miracle baby treated with CRISPR gene-editing therapy at CHOP takes first steps

A miracle baby who was treated with a pioneering gene-therapy at Children’s Hospital of Philadelphia has reached a major milestone as he took his first steps.

KJ Muldoon was the first patient in the world to receive personalized gene-editing therapy, also known as CRISPR.

The advancement, developed by doctors in Philadelphia, saved him from a potentially fatal disease, allowing ammonia to build up in his body…

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